The low efficiency of conventional vectors used for genetic medicines often means delivering them at high doses and by suboptimal routes, leading to inflammation, toxic side effects and limited ...

Barcelona, Spain: Researchers have shown for the first time that it is possible for a specially-designed ‘mini-protein’ to deliver a radiation dose directly to tumour cells expressing a protein on ...

Gene therapies are unlocking new drug targets that were previously thought undruggable. Covering modalities like ASOs, siRNA, saRNA, mRNA, and ADARs, each with different mechanisms of action, gene ...